成人论坛

A toddler with a rare and devastating inherited condition has become the first child to be treated in the UK with a lifesaving gene therapy. The drug, called Libmeldy, is the most expensive medicine in Europe, costing nearly three million pounds ($3.48m) per patient. For the family it is bittersweet as only one of the two children can be saved. The 成人论坛's medical editor Fergus Walsh has followed the treatment at Royal Manchester Children's Hospital over several months and has this exclusive report.